Gene therapy for sickle cell disease passes key preclinical test — Harvard Gazette

A precision-engineered gene therapy virus, inserted into blood stem cells that are then transplanted, markedly reduced sickle-induced red-cell damage in mice with sickle cell disease, researchers from Dana-Farber/Boston Children’s Cancer and Blood Disorders Center reported in the Journal of Clinical Investigation.

Transformative' gene therapies could reduce sickle cell disease complications. Here's how Massachusetts played a part.

Gene editing shows promise as sickle cell therapy — Harvard Gazette

gene therapy, The Stem Cellar

Sickle cell treatment marks gene therapy milestone

Frontiers Clinical Utility of the Addition of Molecular Genetic Testing to Newborn Screening for Sickle Cell Anemia

Денис Савин (@withoutpassions) / X

New study shows promising evidence for sickle cell gene therapy - UChicago Medicine

New study shows promising evidence for sickle cell gene therapy - UChicago Medicine

Health Archives — Page 34 of 107 — Harvard Gazette

New study shows promising evidence for sickle cell gene therapy - UChicago Medicine

The Stem Cellar, The Official Blog of CIRM, California's Stem Cell Agency

F.D.A. Approves 2 Sickle Cell Treatments, One Using CRISPR Gene Editing - The New York Times

SEC Filing CRISPR Therapeutics